Retrieve available abstracts of 92 articles: HTML format
Single Articles
September 2025
NAKAO S Romiplostim for aplastic anemia: beyond an eltrombopag alternative.
Haematologica. 2025 Sep 4. doi: 10.3324/haematol.2025.288632. PubMedAbstract available
July 2025
BORDBAR M, Faghihi A, Zekavat OR, Shahriari M, et al Safety and efficacy of romiplostim in children with acquired aplastic anemia who
are naive to immunosuppressive therapy.
Haematologica. 2025 Jul 24. doi: 10.3324/haematol.2025.288078. PubMedAbstract available
PRATA PH, Eikema DJ, Piepenbroek B, Kulasekararaj A, et al Hematopoietic stem cell transplantation is effective in achieving long-term
survival for post-aplastic anemia myeloid neoplasms: the EBMT Severe Aplastic
Anemia Report.
Haematologica. 2025 Jul 3. doi: 10.3324/haematol.2024.287205. PubMedAbstract available
June 2025
MOZESSOHN L, Buckstein R Should we move past erythropoietin-stimulating agent monotherapy in lower-risk
myelodysplastic syndromes?
Haematologica. 2025 Jun 26. doi: 10.3324/haematol.2025.288157. PubMedAbstract available
BERNAUDIN F, Arnaud C, Kamdem A, Youn J, et al Early detection and management of extracranial arteriopathy reduces the incidence
of silent cerebral infarcts in sickle cell anemia: a long-term prospective cohort
study.
Haematologica. 2025 Jun 26. doi: 10.3324/haematol.2025.287720. PubMedAbstract available
MEI C, Xu G, Zheng C, Xie Y, et al Recombinant human erythropoietin plus all-trans retinoic acid and testosterone
undecanoate for the treatment of anemia in patients with lower-risk
myelodysplastic syndromes: a multicenter, single-arm, prospective trial.
Haematologica. 2025 Jun 12. doi: 10.3324/haematol.2024.287055. PubMedAbstract available
BEYAR-KATZ O, Rejeski K, Shouval R Immune effector cell-associated hematotoxicity: mechanisms, clinical
manifestations, and management strategies.
Haematologica. 2025;110:1254-1268. PubMedAbstract available
May 2025
PARISI L, Escher R Myopathy, lactic acidosis and sideroblastic anemia syndrome 1 (MLASA1) : clinical
hallmarks in a large pedigree with a novel PUS1 R144Q mutation, remarkable
response to somatropin, and review of the literature.
Haematologica. 2025 May 29. doi: 10.3324/haematol.2025.287393. PubMedAbstract available
OVED JH, Bacigalupo A, DeZern AE Towards graft-versus-host disease-free alternative donor transplant platforms for
patients with acquired aplastic anemia.
Haematologica. 2025 May 29. doi: 10.3324/haematol.2024.286544. PubMedAbstract available
BRANDSEN RP, Diederen RMH, Kocabas G, Nur E, et al Clinical and laboratory risk factors for sickle cell retinopathy and maculopathy:
a scoping review of the current evidence.
Haematologica. 2025;110:1092-1104. PubMedAbstract available
April 2025
SHAMIR G, Rouvio O, Reiner-Benaim A Prognostic and biological characteristics associated with multiple myeloma
presenting only with anemia.
Haematologica. 2025 Apr 30. doi: 10.3324/haematol.2024.286457. PubMedAbstract available
DANIELS DE, Hawksworth J, El Hoss S, Oyawoye FO, et al Optimizing CRISPR methodology for precise gene editing in the erythroid cell line
BEL-A with high efficiency generation of a sickle cell anemia model.
Haematologica. 2025 Apr 10. doi: 10.3324/haematol.2024.287221. PubMedAbstract available
March 2025
KOO J, Snyder AJ, Campbell K, Miller E, et al Hepatocyte senescence and persistent liver injury in Fanconi anemia.
Haematologica. 2025 Mar 6. doi: 10.3324/haematol.2024.287096. PubMedAbstract available
SCOURFIELD LEA, Nardo-Marino A, Williams TN, Rees DC, et al Infections in sickle cell disease.
Haematologica. 2025;110:546-561. PubMedAbstract available
GOTARDO EMF, Torres LS, Zaidan BC, Gushiken LFS, et al Targeting P-selectin and interleukin-1beta in mice with sickle cell disease: effects
on vaso-occlusion, liver injury and organ iron deposition.
Haematologica. 2025;110:725-738. PubMedAbstract available
January 2025
QUINN CT, Ware RE The modern use of hydroxyurea for children with sickle cell anemia.
Haematologica. 2025 Jan 9. doi: 10.3324/haematol.2023.284633. PubMedAbstract available
STEINBERG-SHEMER O, Goldberg TA, Yacobovich J, Levin C, et al Erratum to: Characterization and genotype-phenotype correlation of patients with
Fanconi anemia in a multi-ethnic population.
Haematologica. 2025;110:264-265. PubMed
December 2024
EL HOSS S, Shangaris P, Brewin J, Psychogyiou ME, et al Reduced GATA1 levels are associated with ineffective erythropoiesis in sickle
cell anemia.
Haematologica. 2024 Dec 5. doi: 10.3324/haematol.2024.286010. PubMedAbstract available
November 2024
OLIVIER E, Zhang S, Yan Z, Bouhassira EE, et al Erratum to: Stem cell factor and erythropoietin-independent production of
cultured reticulocytes.
Haematologica. 2024;109:3829-3831. PubMed
October 2024
SALIMBENI AF, De Rosa L, Volpato A, Viaro F, et al Posterior cerebral circulation in children with sickle cell anemia: an uncharted
territory.
Haematologica. 2024 Oct 24. doi: 10.3324/haematol.2024.285773. PubMedAbstract available
ABBOUD MR Cerebral vasculopathy in patients with sickle cell disease and stroke: now you
see it, now you don't.
Haematologica. 2024;109:3108-3109. PubMed
LINGUET SL, Verlhac S, Missud F, Holvoet-Vermaut L, et al Stroke without cerebral arteriopathy in sickle cell disease children: causes and
treatment.
Haematologica. 2024;109:3346-3356. PubMedAbstract available
September 2024
RUSSO G, Colombatti R Are we ready for new strategies to prevent stroke in children with sickle cell
disease?
Haematologica. 2024;109:2767-2768. PubMed
PANTOPOULOS K Oral iron supplementation: new formulations, old questions.
Haematologica. 2024;109:2790-2801. PubMedAbstract available
DE LIGT LA, Fijnvandraat K, Biemond BJ, Heijboer H, et al Withholding transfusion therapy in children with sickle cell disease with
abnormal transcranial Doppler and normal magnetic resonance angiography: a
retrospective analysis.
Haematologica. 2024;109:3009-3012. PubMed
August 2024
QUEIROZ DMM, Braga LLC, Rocha GA, Batista SA, et al Infection by Helicobacter pylori cytotoxin-A-associated antigen-positive strains
is associated with iron deficiency anemia in a longitudinal birth cohort in
Brazil.
Haematologica. 2024 Aug 22. doi: 10.3324/haematol.2024.285446. PubMedAbstract available
MOUGIN L, Riccetti M, Merlet AN, Bartolucci P, et al Endurance training improves oxygen uptake/demand mismatch, metabolic flexibility
and recovery in patients with sickle cell disease.
Haematologica. 2024;109:2628-2638. PubMedAbstract available
KUMAR J, Lewis NE, Sherpa S, Londono D, et al Diagnostic challenges and proposed classification of myeloid neoplasms with
overlapping features of thrombocytosis, ring sideroblasts and concurrent del(5q)
and SF3B1 mutations.
Haematologica. 2024;109:2676-2681. PubMed
PIEHLER AP, Truger M, Kozik JH, Weissmann S, et al Classical meets malignant hematology: a case of acquired epsilongammadeltabeta-thalassemia in
clonal hematopoiesis.
Haematologica. 2024;109:2745-2748. PubMed
FARRUKH F, Abdelmagid M, Mangaonkar A, Patnaik M, et al Prognostic impact of SF3B1 mutation and multilineage dysplasia in myelodysplastic
syndromes with ring sideroblasts: a Mayo Clinic study of 170 informative cases.
Haematologica. 2024;109:2525-2532. PubMedAbstract available
D'ALESSANDRO A, Le K, Lundt M, Li Q, et al Functional and multi-omics signatures of mitapivat efficacy upon activation of
pyruvate kinase in red blood cells from patients with sickle cell disease.
Haematologica. 2024;109:2639-2652. PubMedAbstract available
July 2024
WANG P, Jiang W, Lai T, Liu Q, et al Germline variants in acquired aplastic anemia: current knowledge and future
perspectives.
Haematologica. 2024 Jul 11. doi: 10.3324/haematol.2023.284312. PubMedAbstract available
BROCCIA MV, Vergier J, Benoit A, Huguenin Y, et al Pubertal development of transfusion-dependent thalassemia patients in the era of
oral chelation with deferasirox: results from the French registry.
Haematologica. 2024;109:2271-2276. PubMed
June 2024
MATTE A, Federti E, Recchiuti A, Hamza M, et al Epeleuton, a novel synthetic omega-3 fatty acid, reduces hypoxia/ reperfusion stress
in a mouse model of sickle cell disease.
Haematologica. 2024;109:1918-1932. PubMedAbstract available
May 2024
QUDEIMAT A, Suryaprakash S, Madden R, Srinivasan A, et al Reduced toxicity conditioning for hematopoietic stem cell transplantation in
children with Diamond-Blackfan anemia.
Haematologica. 2024 May 30. doi: 10.3324/haematol.2024.285147. PubMedAbstract available
KOO J, Howell JC, Hornung L, Sabulski A, et al Infrequent fractures and resilient bone mineral density: bone health in patients
with Fanconi anemia.
Haematologica. 2024 May 30. doi: 10.3324/haematol.2024.285612. PubMedAbstract available
ZAHR RS, Rashkin SR, Ruiz MA, Elsherif L, et al Soluble urokinase plasminogen activator receptor is associated with kidney
disease and its progression in sickle cell anemia.
Haematologica. 2024 May 2. doi: 10.3324/haematol.2023.284920. PubMedAbstract available
PECKER LH, Federspiel J Sickle cell disease, pregnancy, and COVID-19 in France: plus ca change.
Haematologica. 2024;109:1328-1330. PubMed
KAMINSKI TW, Katoch O, Li Z, Hanway CB, et al Impaired hemoglobin clearance by sinusoidal endothelium promotes vaso-occlusion
and liver injury in sickle cell disease.
Haematologica. 2024;109:1535-1550. PubMedAbstract available
JOSEPH L, De Luna G, Bernit E, Cougoul P, et al A study of 28 pregnant women with sickle cell disease and COVID-19: elevated
maternal and fetal morbidity rates.
Haematologica. 2024;109:1562-1565. PubMed
April 2024
CONNOR MP, Prathapa N, Frey NV, Gill SI, et al Hypomethylating agents are associated with high rates of hematologic toxicity in
patients with secondary myeloid neoplasms developing after acquired aplastic
anemia.
Haematologica. 2024 Apr 18. doi: 10.3324/haematol.2024.285275. PubMedAbstract available
GLENTHOJ A Beyond adenosine triphosphate: unveiling the pleiotropic effects of pyruvate
kinase activation in sickle cell anemia.
Haematologica. 2024 Apr 18. doi: 10.3324/haematol.2024.285390. PubMedAbstract available
OLIVIER E, Zhang S, Yan Z, Bouhassira EE, et al Stem cell factor and erythropoietin-independent production of cultured
reticulocytes.
Haematologica. 2024 Apr 11. doi: 10.3324/haematol.2023.284427. PubMedAbstract available
DENIS M, Swartzrock L, Willner H, Bubb QR, et al Hematopoiesis post anti-CD117 monoclonal antibody treatment in wild-type and
Fanconi anemia settings.
Haematologica. 2024 Apr 4. doi: 10.3324/haematol.2023.284275. PubMedAbstract available
BOSE P, Masarova L, Pemmaraju N, Bledsoe SD, et al Sotatercept for anemia of myelofibrosis: a phase II investigator-initiated study.
Haematologica. 2024 Apr 4. doi: 10.3324/haematol.2023.284078. PubMed
DUBEY RK, Vats R, Brzoska T, Kaminski TW, et al Subcutaneous injection of IHP-102 prevents lung vaso-occlusion in sickle cell
disease mice.
Haematologica. 2024;109:1259-1263. PubMed
March 2024
ZHANG Q, Lin P, Mao A, Liu Y, et al An unusual case of thalassemia intermedia with inheritable complex repeats
detected by single-molecule optical mapping.
Haematologica. 2024;109:1000-1006. PubMed
AL-SAMKARI H, Grace RF, Glenthoj A, Andres O, et al Bone mineral density in adult patients with pyruvate kinase deficiency on
long-term mitapivat treatment.
Haematologica. 2024;109:963-967. PubMed
RISITANO AM, Frieri C Understanding pharmacological complement inhibition in paroxysmal nocturnal
hemoglobinuria.
Haematologica. 2024;109:704-708. PubMed
KULASEKARARAJ AG, Lehtinen AE, Forsyth C, Gandhi S, et al Phase II trials of zilucoplan in paroxysmal nocturnal hemoglobinuria.
Haematologica. 2024;109:929-935. PubMed
February 2024
LU Y, Zhu Q, Wang Y, Luo M, et al Enhancement of PRMT6 binding to a novel germline GATA1 mutation associated with
congenital anemia.
Haematologica. 2024 Feb 22. doi: 10.3324/haematol.2023.284183. PubMedAbstract available
XU ZL, Xu LP, Zhang YC, Zhou YH, et al The outcome and predictive model of allogeneic hematopoietic stem cell
transplantation among elderly patients with severe aplastic anemia from the
Chinese Blood and Marrow Transplant Registry Group.
Haematologica. 2024 Feb 1. doi: 10.3324/haematol.2023.284581. PubMedAbstract available
LIU Y, Zhuang Y, Chen J, Zhong Z, et al Quantitative evaluation of the clinical severity of hemoglobin H disease in a
cohort of 591 patients using a scoring system based on regression analysis.
Haematologica. 2024;109:632-638. PubMed
January 2024
FOUDA RT, Cherukury HM, Kiven SB, Garcia NR, et al Colchicine reduces inflammation in a humanized transgenic murine model of sickle
cell disease.
Haematologica. 2024;109:308-311. PubMed
THILAKARATHNE S, Jayaweera UP, Premawardhena A Unresolved laboratory issues of the heterozygous state of beta-thalassemia: a
literature review.
Haematologica. 2024;109:23-32. PubMedAbstract available
December 2023
RAJPUT RV, Shah V, Shalhoub RN, West-Mitchell K, et al Granulocyte transfusions in severe aplastic anemia.
Haematologica. 2023 Dec 7. doi: 10.3324/haematol.2023.283826. PubMedAbstract available
D'ALESSANDRO A, Nouraie SM, Zhang Y, Cendali F, et al Metabolic signatures of cardiorenal dysfunction in plasma from sickle cell
patients as a function of therapeutic transfusion and hydroxyurea treatment.
Haematologica. 2023;108:3418-3432. PubMedAbstract available
COLOMBATTI R, Casale M Early splenectomy in sickle cell disease: another piece of the puzzle.
Haematologica. 2023;108:3197-3198. PubMed
YAMASHITA D, Muramatsu H, Narita A, Wakamatsu M, et al Hematological abnormalities in Jacobsen syndrome: cytopenia of varying severities
and morphological abnormalities in peripheral blood and bone marrow.
Haematologica. 2023;108:3438-3443. PubMed
November 2023
ESPERTI S, Nader E, Stier A, Boisson C, et al Increased retention of functional mitochondria in mature sickle red blood cells
is associated with increased sickling tendency, hemolysis and oxidative stress.
Haematologica. 2023;108:3086-3094. PubMedAbstract available
TEFFERI A, Pardanani A, Gangat N Momelotinib (JAK1/JAK2/ACVR1 inhibitor): mechanism of action, clinical trial
reports, and therapeutic prospects beyond myelofibrosis.
Haematologica. 2023;108:2919-2932. PubMedAbstract available
October 2023
GUERRA A, Parhiz H, Rivella S Novel potential therapeutics to modify iron metabolism and red cell synthesis in
diseases associated with defective erythropoiesis.
Haematologica. 2023;108:2582-2593. PubMedAbstract available
KALLEDA N, Flace A, Altermatt P, Ingoglia G, et al Ferroportin inhibitor vamifeport ameliorates ineffective erythropoiesis in a
mouse model of beta-thalassemia with blood transfusions.
Haematologica. 2023;108:2703-2714. PubMedAbstract available
VERSTOVSEK S, Foltz L, Gupta V, Hasserjian R, et al Safety and efficacy of zinpentraxin alfa as monotherapy or in combination with
ruxolitinib in myelofibrosis: stage I of a phase II trial.
Haematologica. 2023;108:2730-2742. PubMedAbstract available
September 2023
DEZERN AE, Zahurak M, Jones RJ, Brodsky RA, et al Uniform conditioning regardless of donor in bone marrow transplantation for
severe aplastic anemia.
Haematologica. 2023 Sep 7. doi: 10.3324/haematol.2023.284022. PubMedAbstract available
BROUSSE V, Bernaudin F, Melaine A, Goguillot M, et al Severity and burden of sickle cell disease in France: a nationwide real-world
study.
Haematologica. 2023;108:2476-2486. PubMedAbstract available
MATTE A, Kosinski PA, Federti E, Dang L, et al Mitapivat, a pyruvate kinase activator, improves transfusion burden and reduces
iron overload in beta-thalassemic mice.
Haematologica. 2023;108:2535-2541. PubMed
August 2023
GRIFFIN M, Eikema DJ, Verheggen I, Kulagin A, et al SARS-CoV-2 vaccination in 361 non-transplanted patients with aplastic anemia
and/or paroxysmal nocturnal hemoglobinuria.
Haematologica. 2023 Aug 16. doi: 10.3324/haematol.2023.283863. PubMed
CIUDAD M, Ouandji S, Lamarthee B, Cladiere C, et al Regulatory T-cell dysfunctions are associated with increase in tumor necrosis
factor alpha in autoimmune hemolytic anemia and participate in Th17 polarization.
Haematologica. 2023 Aug 3. doi: 10.3324/haematol.2023.282859. PubMedAbstract available
July 2023
BACIGALUPO A Long term survivors in severe aplastic anemia: standard mortality rates now
comparable to controls?
Haematologica. 2023 Jul 13. doi: 10.3324/haematol.2023.283523. PubMedAbstract available
ALKOBTAWI M, Sbeih M, Souaid K, Ngo QT, et al Contribution of fetal microchimeric cells to maternal wound healing in sickle
cell ulcers.
Haematologica. 2023;108:1920-1933. PubMedAbstract available
June 2023
DROR Y Correcting the aberrant Fanconi anemia transcriptional program by gene therapy.
Haematologica. 2023 Jun 8. doi: 10.3324/haematol.2023.283031. PubMedAbstract available
NAKAMURA R, Patel BA, Kim S, Wong FL, et al Conditional survival and standardized mortality ratios of patients with severe
aplastic anemia surviving at least one year after hematopoietic cell
transplantation or immunosuppressive therapy.
Haematologica. 2023 Jun 1. doi: 10.3324/haematol.2023.282781. PubMedAbstract available
May 2023
MECHRAOUI A, Ithier G, Pages J, Haouari Z, et al Early splenectomy in a large cohort of children with sickle cell anemia: risks
and consequences.
Haematologica. 2023 May 25. doi: 10.3324/haematol.2022.282556. PubMedAbstract available
LIU Y, Schmiderer L, Hjort M, Lang S, et al Engineered human Diamond-Blackfan anemia disease model confirms therapeutic
effects of clinically applicable lentiviral vector at single-cell resolution.
Haematologica. 2023 May 18. doi: 10.3324/haematol.2022.282068. PubMedAbstract available
PAGLIUCA S, Kulasekararaj AG, Eikema DJ, Piepenbroek B, et al Current use of androgens in bone marrow failure disorders: a report from the
Severe Aplastic Anemia Working Party of the European Society of Blood and Marrow
Transplantation.
Haematologica. 2023 May 18. doi: 10.3324/haematol.2023.282935. PubMedAbstract available
FEDERTI E, Vinchi F, Iatcenko I, Ghigo A, et al Duality of Nrf2 in iron-overload cardiomyopathy.
Haematologica. 2023;108:1335-1348. PubMedAbstract available
ATAGA KI, Zhou Q, Saraf SL, Hankins JS, et al Sex differences in progression of kidney disease in sickle cell disease.
Haematologica. 2023;108:1436-1441. PubMed
WANG L, Liu S, Luo J, Mo Q, et al Targeting a thrombopoietin-independent strategy in the discovery of a novel
inducer of megakaryocytopoiesis, DMAG, for the treatment of thrombocytopenia.
Haematologica. 2023;108:1394-1411. PubMedAbstract available
KULASEKARARAJ A, Brodsky R, Kulagin A, Jang JH, et al Biosimilars in rare diseases: a focus on paroxysmal nocturnal hemoglobinuria.
Haematologica. 2023;108:1232-1243. PubMedAbstract available
April 2023
ROSATO BE, Marra R, Del Giudice F, Nostroso A, et al One gene, two opposite phenotypes: a case report of hereditary anemia due to a
loss-offunction variant in the EPAS1 gene.
Haematologica. 2023 Apr 27. doi: 10.3324/haematol.2022.282457. PubMedAbstract available
LASAGA M, Rio P, Vilas-Zornoza A, Planell N, et al Gene therapy restores the transcriptional program of hematopoietic stem cells in
Fanconi anemia.
Haematologica. 2023 Apr 6. doi: 10.3324/haematol.2022.282418. PubMedAbstract available
NARDO-MARINO A, Brousse V Splenectomy in sickle cell disease: do benefits outweigh risks?
Haematologica. 2023;108:954-955. PubMed
PINTO VM, Gianesin B, Piel FB, Longo F, et al Morbidity and mortality of sickle cell disease patients is unaffected by
splenectomy: evidence from three decades of follow-up in a high-income setting.
Haematologica. 2023;108:1158-1162. PubMed
March 2023
DEVILLIER R, Eikema DJ, Dufour C, Aljurf M, et al Graft-versus-host disease and relapse/rejection-free survival after allogeneic
transplantation for idiopathic severe aplastic anemia: a comprehensive analysis
from the SAAWP of the EBMT.
Haematologica. 2023 Mar 23. doi: 10.3324/haematol.2022.281876. PubMedAbstract available
KOO J, Grom-Mansencal I, Howell JC, Rios JM, et al Gonadal function in pediatric Fanconi anemia patients treated with hematopoietic
stem cell transplant.
Haematologica. 2023 Mar 9. doi: 10.3324/haematol.2022.282094. PubMedAbstract available
GALINDO-NAVARRO P, Delgado-Garcia A, Rodriguez-Gil MA, Puerta-Puerta JM, et al Venetoclax for treating refractory autoimmune hemolytic anemia in chronic
lymphocytic leukemia: report of two cases in Spain.
Haematologica. 2023 Mar 2. doi: 10.3324/haematol.2022.281850. PubMedAbstract available
JASH A, Howie HL, Hay AM, Luckey CJ, et al Identification of multiple genetic loci associated with red blood cell
alloimmunization in mice.
Haematologica. 2023;108:905-908. PubMed
FALGUIERE C, Allali S, Khazem B, Kamdem A, et al Delayed hemolytic transfusion reaction in children with sickle cell disease:
first 5-year retrospective study in mainland France.
Haematologica. 2023;108:889-894. PubMed
PINCEZ T, Lo KS, D'Orengiani APHD, Garrett ME, et al Variation and impact of polygenic hematologic traits in monogenic sickle cell
disease.
Haematologica. 2023;108:870-881. PubMedAbstract available
CONRAN N Pain mechanisms in sickle cell disease. Are we closer to a breakthrough?
Haematologica. 2023;108:663-664. PubMed
KHASABOVA IA, Gable J, Johns M, Khasabov SG, et al Inhibition of DAGLbeta as a therapeutic target for pain in sickle cell disease.
Haematologica. 2023;108:859-869. PubMedAbstract available