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Articles published in N Engl J Med

Retrieve available abstracts of 94 articles:
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Single Articles


    May 2024
  1. FRANGOUL H, Locatelli F, Sharma A, Bhatia M, et al
    Exagamglogene Autotemcel for Severe Sickle Cell Disease.
    N Engl J Med. 2024;390:1649-1662.
    PubMed     Abstract available


  2. LOCATELLI F, Lang P, Wall D, Meisel R, et al
    Exagamglogene Autotemcel for Transfusion-Dependent beta-Thalassemia.
    N Engl J Med. 2024;390:1663-1676.
    PubMed     Abstract available


  3. DALEY GQ
    Welcoming the Era of Gene Editing in Medicine.
    N Engl J Med. 2024;390:1642-1645.
    PubMed    


  4. MCCUNE JM, Kiem HP
    Extending Gene Medicines to All in Need.
    N Engl J Med. 2024;390:1721-1722.
    PubMed    


    April 2024
  5. LAM WK, Yip SF
    Drug-Induced Oxidative Hemolysis.
    N Engl J Med. 2024;390:1513.
    PubMed    


    March 2024
  6. PEFFAULT DE LATOUR R, Roth A, Kulasekararaj AG, Han B, et al
    Oral Iptacopan Monotherapy in Paroxysmal Nocturnal Hemoglobinuria.
    N Engl J Med. 2024;390:994-1008.
    PubMed     Abstract available


  7. CARSON JL, Brooks MM, Hebert PC
    Transfusion Strategy in Myocardial Infarction and Anemia. Reply.
    N Engl J Med. 2024;390:961-962.
    PubMed    


  8. KHAN MS, Spertus JA, Chan PS
    Transfusion Strategy in Myocardial Infarction and Anemia.
    N Engl J Med. 2024;390:960-961.
    PubMed    


  9. CHAPALAIN X, Aubron C
    Transfusion Strategy in Myocardial Infarction and Anemia.
    N Engl J Med. 2024;390:960.
    PubMed    


    December 2023
  10. FREEDMAN SB, van de Kar NCAJ, Tarr PI
    Shiga Toxin-Producing Escherichia coli and the Hemolytic-Uremic Syndrome. Reply.
    N Engl J Med. 2023;389:2500.
    PubMed    


  11. JACOBS FM
    Shiga Toxin-Producing Escherichia coli and the Hemolytic-Uremic Syndrome.
    N Engl J Med. 2023;389:2499-2500.
    PubMed    


  12. NORIS M, Remuzzi G
    Shiga Toxin-Producing Escherichia coli and the Hemolytic-Uremic Syndrome.
    N Engl J Med. 2023;389:2499.
    PubMed    


    November 2023
  13. AZAR SS, Simeone FJ, Jarolimova J, Nussbaum EZ, et al
    Case 37-2023: A 29-Year-Old Man with Sickle Cell Disease and Right Hip Pain.
    N Engl J Med. 2023;389:2088-2096.
    PubMed    


  14. CARSON JL, Brooks MM, Hebert PC, Goodman SG, et al
    Restrictive or Liberal Transfusion Strategy in Myocardial Infarction and Anemia.
    N Engl J Med. 2023 Nov 11. doi: 10.1056/NEJMoa2307983.
    PubMed     Abstract available


  15. ZACHRISON KS, Kamalian S, Sykes DB, Brunker PAR, et al
    Case 34-2023: A 49-Year-Old Woman with Loss of Consciousness and Thrombocytopenia.
    N Engl J Med. 2023;389:1804-1811.
    PubMed    


    October 2023
  16. FREEDMAN SB, van de Kar NCAJ, Tarr PI
    Shiga Toxin-Producing Escherichia coli and the Hemolytic-Uremic Syndrome.
    N Engl J Med. 2023;389:1402-1414.
    PubMed    


    August 2023
  17. SHARMA A, Boelens JJ, Cancio M, Hankins JS, et al
    CRISPR-Cas9 Editing of the HBG1 and HBG2 Promoters to Treat Sickle Cell Disease.
    N Engl J Med. 2023;389:820-832.
    PubMed     Abstract available


  18. FUKUSHIMA H, Matsumoto M
    Cold Agglutinin Syndrome.
    N Engl J Med. 2023;389:642.
    PubMed    


  19. SCHREIBER AR, Santos J, McMahon B, Buckner TW, et al
    A Case of Fetal-Induced Graft-versus-Host Disease.
    N Engl J Med. 2023;389:668-670.
    PubMed    


  20. VAN BAARLE FLF, Biemond BJ, Vlaar APJ
    Platelet Transfusion in Patients with Thrombocytopenia. Reply.
    N Engl J Med. 2023;389:480.
    PubMed    


  21. GILSTAD CW
    Platelet Transfusion in Patients with Thrombocytopenia.
    N Engl J Med. 2023;389:479-480.
    PubMed    


  22. WARNER MA, Hess AS, Frank SM
    Platelet Transfusion in Patients with Thrombocytopenia.
    N Engl J Med. 2023;389:479.
    PubMed    


  23. SHIBUSAWA M, Tanimoto T
    Platelet Transfusion in Patients with Thrombocytopenia.
    N Engl J Med. 2023;389:478-479.
    PubMed    


    June 2023
  24. BLOCK J, Rashkova C, Castanon I, Zoghi S, et al
    Systemic Inflammation and Normocytic Anemia in DOCK11 Deficiency.
    N Engl J Med. 2023 Jun 21. doi: 10.1056/NEJMoa2210054.
    PubMed     Abstract available


    April 2023
  25. VAN DIJCK R, Goncalves Silva AM, Rijneveld AW
    Luspatercept as Potential Treatment for Congenital Sideroblastic Anemia.
    N Engl J Med. 2023;388:1435-1436.
    PubMed    


  26. CHILDERHOSE JE, Cronin RM, Klatt MD, Schamess A, et al
    Treating Chronic Pain in Sickle Cell Disease - The Need for a Biopsychosocial Model.
    N Engl J Med. 2023;388:1349-1351.
    PubMed    


  27. CHASSE M, Fergusson DA, Tinmouth A, Acker JP, et al
    Effect of Donor Sex on Recipient Mortality in Transfusion.
    N Engl J Med. 2023;388:1386-1395.
    PubMed     Abstract available


    March 2023
  28. BURTSCHER M
    Oxygen Delivery in the Treatment of Anemia.
    N Engl J Med. 2023;388:e38.
    PubMed    


  29. LEE AI, Heidari P, Fenves AZ, Bardia A, et al
    Case 8-2023: A 71-Year-Old Woman with Refractory Hemolytic Anemia.
    N Engl J Med. 2023;388:1032-1041.
    PubMed    


    December 2022
  30. MC CAUSLAND FR, Singh AK, Claggett BL, Carroll K, et al
    Daprodustat and On-Treatment Cardiovascular Events in Chronic Kidney Disease. Reply.
    N Engl J Med. 2022;387:2482-2485.
    PubMed    


  31. HUANG C, He Y, Li Y
    Daprodustat and On-Treatment Cardiovascular Events in Chronic Kidney Disease.
    N Engl J Med. 2022;387:2482.
    PubMed    


  32. ROJAS-RIVERA J, Carriazo S, Ortiz A
    Daprodustat and On-Treatment Cardiovascular Events in Chronic Kidney Disease.
    N Engl J Med. 2022;387:2481-2482.
    PubMed    


  33. BUNN HF
    Oxygen Delivery in the Treatment of Anemia.
    N Engl J Med. 2022;387:2362-2365.
    PubMed    


    September 2022
  34. DEBAUN M, Heeney M, Jackson T, Longo D, et al
    Sickle Cell Disease and Gene Therapy - Patient and Physician Perspectives.
    N Engl J Med. 2022;387:e28.
    PubMed    


    August 2022
  35. ZHOU AE, Travassos MA
    Bringing Sickle-Cell Treatments to Children in Sub-Saharan Africa.
    N Engl J Med. 2022;387:488-491.
    PubMed    


    July 2022
  36. WU YW, Comstock BA, Gonzalez FF, Mayock DE, et al
    Trial of Erythropoietin for Hypoxic-Ischemic Encephalopathy in Newborns.
    N Engl J Med. 2022;387:148-159.
    PubMed     Abstract available


  37. NOTARO R, Luzzatto L
    Breakthrough Hemolysis in PNH with Proximal or Terminal Complement Inhibition.
    N Engl J Med. 2022;387:160-166.
    PubMed    


    June 2022
  38. AL-SAMKARI H, Beynon V, van Beers EJ
    Mitapivat versus Placebo for Pyruvate Kinase Deficiency. Reply.
    N Engl J Med. 2022;386:2539.
    PubMed    


  39. SHAH AJ, Schwartz JD, Segovia JC
    Mitapivat versus Placebo for Pyruvate Kinase Deficiency.
    N Engl J Med. 2022;386:2538-2539.
    PubMed    


    April 2022
  40. DI MEGLIO L, Scott A
    Iris Atrophy in Sickle Cell Disease.
    N Engl J Med. 2022;386:1646.
    PubMed    


  41. AL-SAMKARI H, Galacteros F, Glenthoj A, Rothman JA, et al
    Mitapivat versus Placebo for Pyruvate Kinase Deficiency.
    N Engl J Med. 2022;386:1432-1442.
    PubMed     Abstract available


    February 2022
  42. STEINBERG MH
    Fetal-like Hemoglobin in Sickle Cell Anemia.
    N Engl J Med. 2022;386:689-691.
    PubMed    


  43. KANTER J, Walters MC, Krishnamurti L, Mapara MY, et al
    Biologic and Clinical Efficacy of LentiGlobin for Sickle Cell Disease.
    N Engl J Med. 2022;386:617-628.
    PubMed     Abstract available


  44. PAYEN E
    Efficacy and Safety of Gene Therapy for beta-Thalassemia.
    N Engl J Med. 2022;386:488-490.
    PubMed    


  45. LOCATELLI F, Thompson AA, Kwiatkowski JL, Porter JB, et al
    Betibeglogene Autotemcel Gene Therapy for Non-beta(0)/beta(0) Genotype beta-Thalassemia.
    N Engl J Med. 2022;386:415-427.
    PubMed     Abstract available


    January 2022
  46. PATEL A, Tillman BF
    Spur-Cell Hemolytic Anemia.
    N Engl J Med. 2022;386:e6.
    PubMed    


  47. SCHEINBERG P
    A New Standard Immunosuppression Regimen in Severe Aplastic Anemia.
    N Engl J Med. 2022;386:89-90.
    PubMed    


  48. PEFFAULT DE LATOUR R, Kulasekararaj A, Iacobelli S, Terwel SR, et al
    Eltrombopag Added to Immunosuppression in Severe Aplastic Anemia.
    N Engl J Med. 2022;386:11-23.
    PubMed     Abstract available


    December 2021
  49. WILLETT LL, Bromberg GK, Chung R, Leaf RK, et al
    Case 38-2021: A 76-Year-Old Woman with Abdominal Pain, Weight Loss, and Memory Impairment.
    N Engl J Med. 2021;385:2378-2388.
    PubMed    


  50. GOYAL S, Tisdale J, Schmidt M, Kanter J, et al
    Acute Myeloid Leukemia Case after Gene Therapy for Sickle Cell Disease.
    N Engl J Med. 2021 Dec 12. doi: 10.1056/NEJMoa2109167.
    PubMed     Abstract available


  51. PASRICHA SR, Hamadani JD, Biggs BA
    Benefits and Risks of Iron Interventions in Infants in Bangladesh. Reply.
    N Engl J Med. 2021;385:2199.
    PubMed    


  52. TERADA R, Sato T
    Benefits and Risks of Iron Interventions in Infants in Bangladesh.
    N Engl J Med. 2021;385:2198-2199.
    PubMed    


    November 2021
  53. JONASCH E, Donskov F, Iliopoulos O, Rathmell WK, et al
    Belzutifan for Renal Cell Carcinoma in von Hippel-Lindau Disease.
    N Engl J Med. 2021;385:2036-2046.
    PubMed     Abstract available


  54. SINGH AK, Carroll K, McMurray JJV, Solomon S, et al
    Daprodustat for the Treatment of Anemia in Patients Not Undergoing Dialysis.
    N Engl J Med. 2021 Nov 5. doi: 10.1056/NEJMoa2113380.
    PubMed     Abstract available


  55. PARFREY P
    Hypoxia-Inducible Factor Prolyl Hydroxylase Inhibitors for Anemia in CKD.
    N Engl J Med. 2021 Nov 5. doi: 10.1056/NEJMe2117100.
    PubMed    


  56. SINGH AK, Carroll K, Perkovic V, Solomon S, et al
    Daprodustat for the Treatment of Anemia in Patients Undergoing Dialysis.
    N Engl J Med. 2021 Nov 5. doi: 10.1056/NEJMoa2113379.
    PubMed     Abstract available


    October 2021
  57. HILLMEN P, Risitano AM, Peffault de Latour R
    Pegcetacoplan versus Eculizumab in PNH. Reply.
    N Engl J Med. 2021;385:1725-1726.
    PubMed    


  58. GURNARI C, Pagliuca S, Maciejewski JP
    Pegcetacoplan versus Eculizumab in PNH.
    N Engl J Med. 2021;385:1725.
    PubMed    


  59. KULASEKARARAJ AG, Gandhi S, Brodsky RA
    Pegcetacoplan versus Eculizumab in PNH.
    N Engl J Med. 2021;385:1724-1725.
    PubMed    


  60. UEDA Y, Takamori H, Nishimura JI
    Pegcetacoplan versus Eculizumab in PNH.
    N Engl J Med. 2021;385:1723-1724.
    PubMed    


  61. CHERTOW GM, Eckardt KU
    Vadadustat for Anemia in Patients with Dialysis-Dependent or Non-Dialysis-Dependent Chronic Kidney Disease. Reply.
    N Engl J Med. 2021;385:e56.
    PubMed    


  62. BUNN HF
    Vadadustat for Anemia in Patients with Dialysis-Dependent or Non-Dialysis-Dependent Chronic Kidney Disease.
    N Engl J Med. 2021;385:e56.
    PubMed    


  63. HOCK H, Kelly HR, Meyerowitz EA, Frigault MJ, et al
    Case 31-2021: A 21-Year-Old Man with Sore Throat, Epistaxis, and Oropharyngeal Petechiae.
    N Engl J Med. 2021;385:1511-1520.
    PubMed    


  64. BERENTSEN S, Barcellini W
    Autoimmune Hemolytic Anemias.
    N Engl J Med. 2021;385:1407-1419.
    PubMed    


    September 2021
  65. PASRICHA SR, Hasan MI, Braat S, Larson LM, et al
    Benefits and Risks of Iron Interventions in Infants in Rural Bangladesh.
    N Engl J Med. 2021;385:982-995.
    PubMed     Abstract available


  66. PICHAN C, Dhaliwal G, Cusick A, Saint S, et al
    Inadequate Support.
    N Engl J Med. 2021;385:938-944.
    PubMed    


    August 2021
  67. GURNARI C, Rogers HJ
    Copper Deficiency.
    N Engl J Med. 2021;385:640.
    PubMed    


    July 2021
  68. AVELAR RODRIGUEZ D, Orkin J
    An Icteric Tongue.
    N Engl J Med. 2021;385:e16.
    PubMed    


  69. PISCHEL L, Geirsson A, Magaldi J, Martinello RA, et al
    A Brewing Back Pain.
    N Engl J Med. 2021;385:66-72.
    PubMed    


    June 2021
  70. FRANGOUL H, Ho TW, Corbacioglu S
    CRISPR-Cas9 Gene Editing for Sickle Cell Disease and beta-Thalassemia. Reply.
    N Engl J Med. 2021;384:e91.
    PubMed    


  71. MEHTA J
    CRISPR-Cas9 Gene Editing for Sickle Cell Disease and beta-Thalassemia.
    N Engl J Med. 2021;384:e91.
    PubMed    


  72. MEISEL R
    CRISPR-Cas9 Gene Editing for Sickle Cell Disease and beta-Thalassemia.
    N Engl J Med. 2021;384:e91.
    PubMed    


  73. TAHER AT, Musallam KM, Cappellini MD
    beta-Thalassemias. Reply.
    N Engl J Med. 2021;384:2166.
    PubMed    


  74. GEORGALAS I, Petrou P, Kanakis M
    beta-Thalassemias.
    N Engl J Med. 2021;384:2165-2166.
    PubMed    


  75. THONG MK, Ngim CF
    beta-Thalassemias.
    N Engl J Med. 2021;384:2165.
    PubMed    


    May 2021
  76. MUSTJOKI S, Young NS
    Somatic Mutations in "Benign" Disease.
    N Engl J Med. 2021;384:2039-2052.
    PubMed    


  77. GIBBONS MD, Mendoza DP, Waheed A, Barshak MB, et al
    Case 14-2021: A 64-Year-Old Woman with Fever and Pancytopenia.
    N Engl J Med. 2021;384:1849-1857.
    PubMed    


    April 2021
  78. LEVIN A
    Therapy for Anemia in Chronic Kidney Disease - New Interventions and New Questions.
    N Engl J Med. 2021;384:1657-1658.
    PubMed    


  79. ECKARDT KU, Agarwal R, Aswad A, Awad A, et al
    Safety and Efficacy of Vadadustat for Anemia in Patients Undergoing Dialysis.
    N Engl J Med. 2021;384:1601-1612.
    PubMed     Abstract available


  80. CHERTOW GM, Pergola PE, Farag YMK, Agarwal R, et al
    Vadadustat in Patients with Anemia and Non-Dialysis-Dependent CKD.
    N Engl J Med. 2021;384:1589-1600.
    PubMed     Abstract available


  81. ROTH A, Barcellini W, D'Sa S, Miyakawa Y, et al
    Sutimlimab in Cold Agglutinin Disease.
    N Engl J Med. 2021;384:1323-1334.
    PubMed     Abstract available


    March 2021
  82. HILLMEN P, Szer J, Weitz I, Roth A, et al
    Pegcetacoplan versus Eculizumab in Paroxysmal Nocturnal Hemoglobinuria.
    N Engl J Med. 2021;384:1028-1037.
    PubMed     Abstract available


  83. OGUNWOLE SM
    Without Sanctuary.
    N Engl J Med. 2021;384:791-793.
    PubMed    


    February 2021
  84. MENON BS, Teh KH
    Gum Hypertrophy from Cyclosporine.
    N Engl J Med. 2021;384:744.
    PubMed    


  85. TAHER AT, Musallam KM, Cappellini MD
    beta-Thalassemias.
    N Engl J Med. 2021;384:727-743.
    PubMed    


    January 2021
  86. MALECH HL
    Treatment by CRISPR-Cas9 Gene Editing - A Proof of Principle.
    N Engl J Med. 2021;384:286-287.
    PubMed    


  87. WALTERS MC
    Induction of Fetal Hemoglobin by Gene Therapy.
    N Engl J Med. 2021;384:284-285.
    PubMed    


  88. ESRICK EB, Lehmann LE, Biffi A, Achebe M, et al
    Post-Transcriptional Genetic Silencing of BCL11A to Treat Sickle Cell Disease.
    N Engl J Med. 2021;384:205-215.
    PubMed     Abstract available


  89. FRANGOUL H, Altshuler D, Cappellini MD, Chen YS, et al
    CRISPR-Cas9 Gene Editing for Sickle Cell Disease and beta-Thalassemia.
    N Engl J Med. 2021;384:252-260.
    PubMed     Abstract available


    December 2020
  90. KIRPALANI H, Bell EF, Hintz SR, Tan S, et al
    Higher or Lower Hemoglobin Transfusion Thresholds for Preterm Infants.
    N Engl J Med. 2020;383:2639-2651.
    PubMed     Abstract available


  91. MENSAH F, Pilichowska M
    Hemophagocytosis of Sickle Cells.
    N Engl J Med. 2020;383:2571.
    PubMed    


  92. KWAMBAI TK, Dhabangi A, Idro R, Opoka R, et al
    Malaria Chemoprevention in the Postdischarge Management of Severe Anemia.
    N Engl J Med. 2020;383:2242-2254.
    PubMed     Abstract available


    November 2020
  93. MALHOTRA R, Namasivayam M, Ghoshhajra BB, Passeri JJ, et al
    Case 36-2020: A 72-Year-Old Woman with Dark Urine and Weakness.
    N Engl J Med. 2020;383:2066-2076.
    PubMed    


  94. POWER-HAYS A, McGann PT
    When Actions Speak Louder Than Words - Racism and Sickle Cell Disease.
    N Engl J Med. 2020;383:1902-1903.
    PubMed    


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